Clinical trials
Homozygous Familial Hypercholesterolemia trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
67 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2003 | 2 |
| 2005 | 1 |
| 2006 | 2 |
| 2007 | 3 |
| 2008 | 1 |
| 2009 | 1 |
| 2010 | 1 |
| 2011 | 1 |
| 2012 | 2 |
| 2013 | 3 |
| 2014 | 3 |
| 2015 | 4 |
| 2016 | 5 |
| 2017 | 4 |
| 2018 | 5 |
| 2019 | 8 |
| 2020 | 2 |
| 2021 | 1 |
| 2022 | 1 |
| 2023 | 4 |
| 2024 | 4 |
| 2025 | 4 |
| 2026 | 4 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 41 |
| Recruiting | 11 |
| Active, not recruiting | 4 |
| Terminated | 4 |
| Unknown status | 3 |
| Withdrawn | 3 |
| Not yet recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Aegerion Pharmaceuticals, Inc. | 6 |
| Novartis Pharmaceuticals | 6 |
| Regeneron Pharmaceuticals | 5 |
| Kastle Therapeutics, LLC | 4 |
| Amgen | 3 |
| Arrowhead Pharmaceuticals | 3 |
| Beijing Suncadia Pharmaceuticals Co., Ltd | 3 |
| REGENXBIO Inc. | 3 |
| Amryt Pharma | 2 |
| AstraZeneca | 2 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Homozygous Familial Hypercholesterolemia | 67 |
| Hyperlipoproteinemia Type II | 22 |
| Hypercholesterolemia | 14 |
| Dyslipidemias | 9 |
| Genetic Diseases, Inborn | 8 |
| Lipid Metabolism Disorders | 8 |
| Metabolic Diseases | 8 |
| Hyperlipidemias | 7 |
| Atherosclerosis | 6 |
| Cardiovascular Diseases | 6 |
Trials
Showing 26 to 50 of 67. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.