Clinical trials
Completed Homozygous Familial Hypercholesterolemia trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
41 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2003 | 1 |
| 2005 | 1 |
| 2006 | 2 |
| 2007 | 3 |
| 2008 | 1 |
| 2009 | 1 |
| 2011 | 1 |
| 2012 | 2 |
| 2013 | 1 |
| 2014 | 3 |
| 2015 | 3 |
| 2016 | 3 |
| 2017 | 3 |
| 2018 | 3 |
| 2019 | 6 |
| 2020 | 2 |
| 2021 | 1 |
| 2023 | 2 |
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 41 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Regeneron Pharmaceuticals | 5 |
| Aegerion Pharmaceuticals, Inc. | 4 |
| Kastle Therapeutics, LLC | 4 |
| Amgen | 3 |
| Novartis Pharmaceuticals | 3 |
| Amryt Pharma | 2 |
| AstraZeneca | 2 |
| Beijing Suncadia Pharmaceuticals Co., Ltd | 2 |
| Organon and Co | 2 |
| Akeso | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Homozygous Familial Hypercholesterolemia | 41 |
| Hyperlipoproteinemia Type II | 12 |
| Hypercholesterolemia | 9 |
| Hyperlipidemias | 5 |
| Dyslipidemias | 4 |
| Genetic Diseases, Inborn | 4 |
| Metabolic Diseases | 4 |
| Congenital Abnormalities | 3 |
| Hyperlipoproteinemias | 3 |
| Infant, Newborn, Diseases | 3 |
Trials
Showing 26 to 41 of 41. Each trial links to its page on Pharma Observatory.
Recently changed trials
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