Clinical trials
Fabry Disease trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
242 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 1 |
| 2001 | 6 |
| 2002 | 5 |
| 2003 | 5 |
| 2004 | 6 |
| 2005 | 3 |
| 2006 | 6 |
| 2007 | 5 |
| 2008 | 4 |
| 2009 | 6 |
| 2010 | 10 |
| 2011 | 15 |
| 2012 | 8 |
| 2013 | 3 |
| 2014 | 9 |
| 2015 | 9 |
| 2016 | 11 |
| 2017 | 7 |
| 2018 | 12 |
| 2019 | 12 |
| 2020 | 13 |
| 2021 | 14 |
| 2022 | 14 |
| 2023 | 22 |
| 2024 | 9 |
| 2025 | 11 |
| 2026 | 9 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 119 |
| Recruiting | 37 |
| Unknown status | 37 |
| Terminated | 16 |
| Active, not recruiting | 10 |
| Withdrawn | 10 |
| Not yet recruiting | 6 |
| Enrolling by invitation | 3 |
| Available | 2 |
| No longer available | 1 |
| Approved for marketing | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Amicus Therapeutics | 24 |
| Genzyme, a Sanofi Company | 17 |
| Shire | 12 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 11 |
| Chiesi Farmaceutici S.p.A. | 8 |
| CENTOGENE GmbH Rostock | 6 |
| Protalix | 6 |
| Sanofi | 6 |
| Idorsia Pharmaceuticals Ltd. | 5 |
| University Hospital, Bordeaux | 5 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Fabry Disease | 242 |
| Lysosomal Storage Diseases | 18 |
| Stroke | 16 |
| Cardiomyopathy, Hypertrophic | 9 |
| Renal Insufficiency, Chronic | 8 |
| Cardiomyopathies | 7 |
| Gaucher Disease | 7 |
| Proteinuria | 7 |
| Hypertrophy, Left Ventricular | 6 |
| Kidney Diseases | 6 |
Trials
Showing 26 to 50 of 242. Each trial links to its page on Pharma Observatory.
142 more trials match. See them on Pharma Observatory
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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