Clinical trials
Observational Fabry Disease trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
127 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 1 |
| 2001 | 4 |
| 2002 | 2 |
| 2003 | 1 |
| 2004 | 2 |
| 2005 | 1 |
| 2007 | 3 |
| 2008 | 2 |
| 2009 | 4 |
| 2010 | 8 |
| 2011 | 4 |
| 2012 | 3 |
| 2013 | 1 |
| 2014 | 6 |
| 2015 | 5 |
| 2016 | 6 |
| 2017 | 3 |
| 2018 | 6 |
| 2019 | 7 |
| 2020 | 7 |
| 2021 | 8 |
| 2022 | 5 |
| 2023 | 16 |
| 2024 | 6 |
| 2025 | 8 |
| 2026 | 6 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 50 |
| Unknown status | 30 |
| Recruiting | 26 |
| Terminated | 6 |
| Withdrawn | 5 |
| Active, not recruiting | 4 |
| Not yet recruiting | 3 |
| Enrolling by invitation | 3 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| CENTOGENE GmbH Rostock | 6 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 6 |
| Yonsei University | 5 |
| Amicus Therapeutics | 4 |
| IRCCS Azienda Ospedaliero-Universitaria di Bologna | 4 |
| Caroline Michaela Kistorp | 3 |
| Chiesi Farmaceutici S.p.A. | 3 |
| O & O Alpan LLC | 3 |
| Shire | 3 |
| Amicus Therapeutics France SAS | 2 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Fabry Disease | 127 |
| Stroke | 10 |
| Cardiomyopathy, Hypertrophic | 8 |
| Lysosomal Storage Diseases | 7 |
| Renal Insufficiency, Chronic | 7 |
| Cardiomyopathies | 6 |
| Amyloid Neuropathies, Familial | 5 |
| Gaucher Disease | 5 |
| Hypertrophy, Left Ventricular | 5 |
| Rare Diseases | 5 |
Trials
Showing 26 to 50 of 127. Each trial links to its page on Pharma Observatory.
27 more trials match. See them on Pharma Observatory
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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