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Clinical trials

Phase 3 Fabry Disease trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Fabry Disease Phase: Phase 3 Clear all

28 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20082
20091
20101
20113
20151
20161
20173
20185
20191
20211
20225
20231
20262

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed18
Active, not recruiting4
Terminated2
Withdrawn1
Recruiting1
Not yet recruiting1
Unknown status1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Amicus Therapeutics8
Protalix4
Shire4
Idorsia Pharmaceuticals Ltd.3
Chiesi Farmaceutici S.p.A.2
Genzyme, a Sanofi Company2
Sanofi2
Bio Sidus SA1
ISU Abxis Co., Ltd.1
Takeda1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Fabry Disease28
Proteinuria3
Abdominal Pain1
Diarrhea1
Kidney Diseases1
Kidney Failure, Chronic1
Lysosomal Storage Diseases1
Renal Insufficiency1

Trials

Showing 26 to 28 of 28. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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