Clinical trials
Recruiting Fabry Disease trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
37 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 2 |
| 2007 | 1 |
| 2009 | 1 |
| 2010 | 2 |
| 2018 | 1 |
| 2019 | 1 |
| 2020 | 1 |
| 2021 | 2 |
| 2022 | 3 |
| 2023 | 4 |
| 2024 | 7 |
| 2025 | 8 |
| 2026 | 4 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 37 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Chiesi Farmaceutici S.p.A. | 4 |
| Amicus Therapeutics | 3 |
| IRCCS Azienda Ospedaliero-Universitaria di Bologna | 3 |
| Caroline Michaela Kistorp | 2 |
| 4D Molecular Therapeutics | 1 |
| Canadian Fabry Research Consortium | 1 |
| Chiesi Italia | 1 |
| Children's Hospital of Fudan University | 1 |
| Chinese Academy of Medical Sciences, Fuwai Hospital | 1 |
| General University Hospital, Prague | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Fabry Disease | 37 |
| Cardiomyopathy, Hypertrophic | 5 |
| Amyloid Neuropathies, Familial | 4 |
| Cardiomyopathies | 3 |
| Renal Insufficiency, Chronic | 3 |
| Arrhythmogenic Right Ventricular Dysplasia | 2 |
| Cardiomyopathy, Dilated | 2 |
| Cardiovascular Diseases | 2 |
| Cerebral Small Vessel Diseases | 2 |
| Death, Sudden, Cardiac | 2 |
Trials
Showing 51 to 37 of 37. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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