Clinical trials
Phase 1 Fabry Disease trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
13 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2003 | 1 |
| 2011 | 4 |
| 2012 | 1 |
| 2013 | 1 |
| 2014 | 1 |
| 2015 | 1 |
| 2016 | 2 |
| 2021 | 1 |
| 2024 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 11 |
| Recruiting | 1 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Amicus Therapeutics | 5 |
| Bio Sidus SA | 1 |
| Children's Hospital of Fudan University | 1 |
| Genzyme, a Sanofi Company | 1 |
| Green Cross Corporation | 1 |
| Greenovation Biotech GmbH | 1 |
| Idorsia Pharmaceuticals Ltd. | 1 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 1 |
| University Health Network, Toronto | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Fabry Disease | 13 |
| Lysosomal Storage Diseases | 2 |
| Peripheral Nervous System Diseases | 1 |
| Stroke | 1 |
Trials
Showing 76 to 13 of 13. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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