Clinical trials
Charcot-Marie-Tooth Disease trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
40 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2007 | 2 |
| 2010 | 3 |
| 2011 | 1 |
| 2012 | 2 |
| 2013 | 2 |
| 2014 | 3 |
| 2015 | 3 |
| 2016 | 3 |
| 2017 | 4 |
| 2018 | 1 |
| 2019 | 3 |
| 2020 | 2 |
| 2021 | 2 |
| 2022 | 1 |
| 2023 | 1 |
| 2024 | 1 |
| 2025 | 4 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 18 |
| Recruiting | 9 |
| Terminated | 6 |
| Unknown status | 4 |
| Active, not recruiting | 2 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| University of Iowa | 4 |
| Pharnext S.C.A. | 3 |
| Acceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway, NJ USA | 2 |
| Children's Hospital of Philadelphia | 2 |
| NMD Pharma A/S | 2 |
| Nemours Children's Clinic | 2 |
| University of South Florida | 2 |
| Bopha Chrea | 1 |
| Flex Pharma, Inc. | 1 |
| Foundation Fighting Blindness | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Charcot-Marie-Tooth Disease | 40 |
| Neuromuscular Diseases | 5 |
| Amyotrophic Lateral Sclerosis | 4 |
| Hereditary Sensory and Motor Neuropathy | 4 |
| Peripheral Nervous System Diseases | 4 |
| Refsum Disease | 4 |
| Motor Neuron Disease | 3 |
| Muscular Atrophy, Spinal | 3 |
| Adrenoleukodystrophy | 2 |
| Alexander Disease | 2 |
Trials
Showing 51 to 40 of 40. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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