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Clinical trials

Phase 2 Charcot-Marie-Tooth Disease trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Charcot-Marie-Tooth Disease Phase: Phase 2 Clear all

10 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20101
20151
20161
20172
20191
20231
20241
20251

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed5
Terminated3
Not yet recruiting1
Unknown status1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Acceleron Pharma, Inc., a wholly-owned subsidiary of Merck & Co., Inc., Rahway, NJ USA2
Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA)1
Flex Pharma, Inc.1
MedDay Pharmaceuticals SA1
NMD Pharma A/S1
Pharnext S.C.A.1
The Third Xiangya Hospital of Central South University1
University of Rochester1
University of Virginia1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Charcot-Marie-Tooth Disease10
Hereditary Sensory and Motor Neuropathy3
Carpal Tunnel Syndrome1
Genetic Diseases, Inborn1
Median Neuropathy1
Muscle Cramp1
Muscular Dystrophy, Facioscapulohumeral1
Nervous System Diseases1
Nervous System Malformations1
Neurodegenerative Diseases1

Trials

Showing 26 to 10 of 10. Each trial links to its page on Pharma Observatory.

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