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Clinical trials

Completed Dwarfism trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Dwarfism Status: Completed Clear all

57 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20001
20012
20022
20032
20043
20056
20082
20092
20102
20122
20131
20141
20154
20163
20183
20194
20204
20212
20223
20233

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed57

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
BioMarin Pharmaceutical4
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)4
Nemours Children's Clinic4
Children's Hospital Medical Center, Cincinnati3
QED Therapeutics, a BridgeBio company3
Ascendis Pharma A/S2
Istituto Auxologico Italiano2
National Human Genome Research Institute (NHGRI)2
Rabin Medical Center2
Arkansas Children's Hospital Research Institute1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Dwarfism57
Achondroplasia12
Dwarfism, Pituitary11
Turner Syndrome7
Bone Diseases6
Genetic Diseases, Inborn6
Bone Diseases, Developmental5
Musculoskeletal Diseases5
Osteochondrodysplasias5
Mucopolysaccharidosis IV4

Trials

Showing 51 to 57 of 57. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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