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Clinical trials

Phase 1 Fragile X Syndrome trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Fragile X Syndrome Phase: Phase 1 Clear all

14 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20051
20092
20121
20131
20151
20163
20171
20181
20211
20232

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed11
Enrolling by invitation1
Terminated1
Withdrawn1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Children's Hospital Medical Center, Cincinnati3
Stanford University2
Connecta Therapeutics, S.L.1
Guido A. Davidzon, MD, SM1
Healx AI1
Institute for Neurodegenerative Disorders1
Novartis Pharmaceuticals1
Queen's University, Belfast1
Seaside Therapeutics, Inc.1
University Hospital, Tours1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Fragile X Syndrome14
Intellectual Disability4
Autistic Disorder2
Down Syndrome2
Alzheimer Disease1
Angelman Syndrome1
Attention Deficit Disorder with Hyperactivity1
Autism Spectrum Disorder1
Central Nervous System Diseases1
Cognitive Dysfunction1

Trials

Showing 51 to 14 of 14. Each trial links to its page on Pharma Observatory.

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