Clinical trials
Gaucher Disease trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
173 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2002 | 1 |
| 2004 | 1 |
| 2005 | 2 |
| 2006 | 4 |
| 2007 | 5 |
| 2008 | 6 |
| 2009 | 6 |
| 2010 | 7 |
| 2011 | 11 |
| 2012 | 6 |
| 2013 | 5 |
| 2014 | 7 |
| 2015 | 10 |
| 2016 | 4 |
| 2017 | 5 |
| 2018 | 9 |
| 2019 | 10 |
| 2020 | 7 |
| 2021 | 9 |
| 2022 | 10 |
| 2023 | 12 |
| 2024 | 11 |
| 2025 | 1 |
| 2026 | 7 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 91 |
| Recruiting | 23 |
| Unknown status | 22 |
| Active, not recruiting | 10 |
| Withdrawn | 7 |
| Not yet recruiting | 7 |
| Terminated | 6 |
| Enrolling by invitation | 3 |
| No longer available | 1 |
| Suspended | 1 |
| Available | 1 |
| Approved for marketing | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Shire | 14 |
| Genzyme, a Sanofi Company | 12 |
| Sanofi | 11 |
| Pfizer | 8 |
| Shaare Zedek Medical Center | 7 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 6 |
| Takeda | 6 |
| University of Minnesota | 6 |
| Amicus Therapeutics | 5 |
| ISU Abxis Co., Ltd. | 5 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Gaucher Disease | 173 |
| Lysosomal Storage Diseases | 13 |
| Niemann-Pick Diseases | 10 |
| Metabolism, Inborn Errors | 9 |
| Parkinson Disease | 9 |
| Fabry Disease | 7 |
| Leukodystrophy, Metachromatic | 7 |
| Rare Diseases | 7 |
| Wolman Disease | 7 |
| Adrenoleukodystrophy | 6 |
Trials
Showing 51 to 75 of 173. Each trial links to its page on Pharma Observatory.
73 more trials match. See them on Pharma Observatory
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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