Clinical trials
Phase 2 Gaucher Disease trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
18 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2002 | 1 |
| 2006 | 1 |
| 2007 | 1 |
| 2008 | 1 |
| 2009 | 1 |
| 2012 | 1 |
| 2014 | 2 |
| 2015 | 1 |
| 2017 | 1 |
| 2018 | 1 |
| 2019 | 1 |
| 2022 | 1 |
| 2024 | 1 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 11 |
| Unknown status | 3 |
| Active, not recruiting | 1 |
| Not yet recruiting | 1 |
| Recruiting | 1 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Amicus Therapeutics | 3 |
| Genzyme, a Sanofi Company | 2 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 2 |
| Azafaros B.V. | 1 |
| Children's Hospital Medical Center, Cincinnati | 1 |
| Hadassah Medical Organization | 1 |
| National Center for Research Resources (NCRR) | 1 |
| Paul Szabolcs | 1 |
| Peking Union Medical College Hospital | 1 |
| Protalix | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Gaucher Disease | 18 |
| Metabolism, Inborn Errors | 2 |
| Rare Diseases | 2 |
| Sphingolipidoses | 2 |
| Adrenoleukodystrophy | 1 |
| Anemia, Diamond-Blackfan | 1 |
| Anemia, Sickle Cell | 1 |
| Arthritis, Juvenile | 1 |
| Autoimmune Lymphoproliferative Syndrome | 1 |
| Bone Diseases | 1 |
Trials
Showing 51 to 18 of 18. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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