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Clinical trials

Glycogen Storage Disease Type II trials with no applicable phase

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Glycogen Storage Disease Type II Phase: Not applicable Clear all

20 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20041
20051
20091
20131
20152
20162
20172
20191
20201
20211
20221
20231
20242
20252
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed12
Recruiting3
Unknown status3
Active, not recruiting1
Enrolling by invitation1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Centre Hospitalier Universitaire de Nice2
Duke University2
Assistance Publique Hopitaux De Marseille1
Astellas Gene Therapies1
Fondazione Don Carlo Gnocchi ETS1
Genzyme, a Sanofi Company1
LMU Klinikum1
M.A.G.I.C. Clinic LTD1
MidAtlantic Retina1
National Taiwan University Hospital1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Glycogen Storage Disease Type II20
Neuromuscular Diseases3
Lambert-Eaton Myasthenic Syndrome2
Lysosomal Storage Diseases2
Muscular Atrophy, Spinal2
Muscular Dystrophy, Facioscapulohumeral2
Myositis, Inclusion Body2
Polyradiculoneuropathy, Chronic Inflammatory Demyelinating2
Amyotrophic Lateral Sclerosis1
Carbohydrate Metabolism, Inborn Errors1

Trials

Showing 51 to 20 of 20. Each trial links to its page on Pharma Observatory.

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Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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