Clinical trials
Hemoglobinopathies trials in Canada
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
12 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2017 | 1 |
| 2018 | 2 |
| 2021 | 3 |
| 2022 | 3 |
| 2024 | 1 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Active, not recruiting | 4 |
| Completed | 4 |
| Enrolling by invitation | 2 |
| Recruiting | 2 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Vertex Pharmaceuticals Incorporated | 4 |
| Editas Medicine, Inc. | 3 |
| Forma Therapeutics, Inc. | 2 |
| Biossil Inc. | 1 |
| Novartis Pharmaceuticals | 1 |
| Washington University School of Medicine | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Hemoglobinopathies | 12 |
| Hematologic Diseases | 9 |
| Anemia, Sickle Cell | 8 |
| Genetic Diseases, Inborn | 8 |
| beta-Thalassemia | 6 |
| Anemia | 5 |
| Anemia, Hemolytic | 5 |
| Thalassemia | 4 |
| Anemia, Hemolytic, Congenital | 3 |
| Hemolysis | 2 |
Trials
Showing 76 to 12 of 12. Each trial links to its page on Pharma Observatory.
No trials match these filters.
Try a different keyword, or clear a filter.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.