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Clinical trials

Phase 1/2 Hemoglobinopathies trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Hemoglobinopathies Phase: Phase 1/2 Clear all

13 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20011
20052
20132
20142
20172
20191
20211
20221
20251

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Active, not recruiting3
Completed3
Recruiting3
Terminated3
Unknown status1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Bellicum Pharmaceuticals2
Diane George2
Editas Medicine, Inc.2
Washington University School of Medicine2
Ann & Robert H Lurie Children's Hospital of Chicago1
Children's Hospital Medical Center, Cincinnati1
Children's Hospital of Philadelphia1
Nova Laboratories Limited1
Talaris Therapeutics Inc.1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Hemoglobinopathies13
Anemia, Sickle Cell9
Anemia, Aplastic5
Anemia, Diamond-Blackfan4
Bone Marrow Failure Disorders4
Leukemia4
Primary Immunodeficiency Diseases4
Anemia3
Leukemia, Myeloid, Acute3
Lymphoma, Non-Hodgkin3

Trials

Showing 26 to 13 of 13. Each trial links to its page on Pharma Observatory.

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Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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