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Clinical trials

Observational Hemoglobinuria, Paroxysmal trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Hemoglobinuria, Paroxysmal Phase: Observational Clear all

37 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20021
20041
20062
20091
20102
20111
20121
20181
20192
20201
20213
20221
20233
20244
20258
20265

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed14
Recruiting10
Active, not recruiting7
Not yet recruiting2
Unknown status2
Terminated1
Enrolling by invitation1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Alexion Pharmaceuticals, Inc.7
Novartis Pharmaceuticals7
AstraZeneca3
National Heart, Lung, and Blood Institute (NHLBI)2
AO GENERIUM1
Aplastic Anemia and MDS International Foundation1
Assistance Publique - Hôpitaux de Paris1
CARE Pharma Shanghai Ltd.1
Institute of Hematology & Blood Diseases Hospital, China1
International PNH Interest Group1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Hemoglobinuria, Paroxysmal37
Anemia, Aplastic5
Myelodysplastic Syndromes5
Anemia3
Bone Marrow Failure Disorders3
Bone Marrow Diseases2
Hematologic Diseases2
Hemoglobinuria2
Hemolysis2
Leukemia, Large Granular Lymphocytic2

Trials

Showing 26 to 37 of 37. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

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