Clinical trials
Active, not recruiting Hemoglobinuria, Paroxysmal trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
21 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2017 | 1 |
| 2018 | 1 |
| 2020 | 2 |
| 2021 | 2 |
| 2022 | 3 |
| 2023 | 1 |
| 2024 | 4 |
| 2025 | 5 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Active, not recruiting | 21 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Alexion Pharmaceuticals, Inc. | 3 |
| Hoffmann-La Roche | 3 |
| Novartis Pharmaceuticals | 3 |
| AstraZeneca | 1 |
| Bisirna Therapeutics Pte. Ltd. | 1 |
| Chengdu Suncadia Medicine Co., Ltd. | 1 |
| Children's Hospital of Philadelphia | 1 |
| City of Hope Medical Center | 1 |
| Kira Pharmacenticals (US), LLC. | 1 |
| London Health Sciences Centre Research Institute OR Lawson Research Institute of St. Joseph's | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Hemoglobinuria, Paroxysmal | 21 |
| Anemia | 2 |
| Anemia, Aplastic | 1 |
| Anemia, Refractory, with Excess of Blasts | 1 |
| Blast Crisis | 1 |
| Burkitt Lymphoma | 1 |
| Congenital Abnormalities | 1 |
| Congenital Bone Marrow Failure Syndromes | 1 |
| Cytopenia | 1 |
| Dendritic Cell Sarcoma, Interdigitating | 1 |
Trials
Showing 26 to 21 of 21. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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