Clinical trials
Homocystinuria trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
20 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2007 | 1 |
| 2010 | 1 |
| 2015 | 1 |
| 2017 | 1 |
| 2018 | 1 |
| 2019 | 2 |
| 2021 | 2 |
| 2022 | 4 |
| 2023 | 1 |
| 2024 | 4 |
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 9 |
| Recruiting | 3 |
| Enrolling by invitation | 2 |
| Active, not recruiting | 2 |
| Unknown status | 2 |
| Suspended | 1 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Travere Therapeutics, Inc. | 4 |
| Aeglea Biotherapeutics | 1 |
| Assistance Publique - Hôpitaux de Paris | 1 |
| Centre Hospitalier Universitaire de Liege | 1 |
| Hamad Medical Corporation | 1 |
| Hospital de Clinicas de Porto Alegre | 1 |
| King Fahad Armed Forces Hospital | 1 |
| McGill University Health Centre/Research Institute of the McGill University Health Centre | 1 |
| National Center for Research Resources (NCRR) | 1 |
| RTI International | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Homocystinuria | 20 |
| Tyrosinemias | 4 |
| Argininosuccinic Aciduria | 3 |
| Biotinidase Deficiency | 3 |
| Carbamoyl-Phosphate Synthase I Deficiency Disease | 3 |
| Citrullinemia | 3 |
| Hyperargininemia | 3 |
| Maple Syrup Urine Disease | 3 |
| Metabolism, Inborn Errors | 3 |
| Ornithine Carbamoyltransferase Deficiency Disease | 3 |
Trials
Showing 51 to 20 of 20. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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