Skip to content

Clinical trials

Observational Homocystinuria trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Homocystinuria Phase: Observational Clear all

8 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20171
20181
20191
20222
20241
20251

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed4
Active, not recruiting1
Enrolling by invitation1
Recruiting1
Unknown status1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Centre Hospitalier Universitaire de Liege1
King Fahad Armed Forces Hospital1
National Center for Research Resources (NCRR)1
RTI International1
Travere Therapeutics, Inc.1
University Children's Hospital, Zurich1
University of Lausanne1
West Kazakhstan Medical University1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Homocystinuria8
Argininosuccinic Aciduria3
Biotinidase Deficiency3
Carbamoyl-Phosphate Synthase I Deficiency Disease3
Citrullinemia3
Hyperargininemia3
Ornithine Carbamoyltransferase Deficiency Disease3
Tyrosinemias3
Anemia, Sickle Cell2
Congenital Hyperinsulinism2

Trials

Showing 76 to 8 of 8. Each trial links to its page on Pharma Observatory.

No trials match these filters.

Try a different keyword, or clear a filter.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.