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Clinical trials

Phase 2 Infant, Newborn, Diseases trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Infant, Newborn, Diseases Phase: Phase 2 Clear all

12 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20072
20092
20101
20121
20141
20201

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed10
Recruiting1
Terminated1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Vertex Pharmaceuticals Incorporated3
Kastle Therapeutics, LLC2
National Center for Research Resources (NCRR)2
Alexion Pharmaceuticals, Inc.1
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)1
Johns Hopkins Bloomberg School of Public Health1
Universitaire Ziekenhuizen KU Leuven1
Washington University School of Medicine1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Infant, Newborn, Diseases12
Genetic Diseases, Inborn6
Cystic Fibrosis3
Lipid Metabolism Disorders3
Lipid Metabolism, Inborn Errors3
Lung Diseases3
Metabolic Diseases3
Metabolism, Inborn Errors3
Pancreatic Diseases3
Respiratory Tract Diseases3

Trials

Showing 51 to 12 of 12. Each trial links to its page on Pharma Observatory.

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Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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