Clinical trials
Phase 2 Mucopolysaccharidosis I trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
8 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2002 | 1 |
| 2004 | 1 |
| 2008 | 1 |
| 2009 | 1 |
| 2014 | 2 |
| 2018 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 5 |
| Active, not recruiting | 1 |
| Recruiting | 1 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Masonic Cancer Center, University of Minnesota | 5 |
| Genzyme, a Sanofi Company | 1 |
| Magenta Therapeutics, Inc. | 1 |
| Paul Szabolcs | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis I | 8 |
| Leukodystrophy, Globoid Cell | 5 |
| Leukodystrophy, Metachromatic | 5 |
| Mucopolysaccharidosis VI | 4 |
| alpha-Mannosidosis | 4 |
| Aspartylglucosaminuria | 3 |
| Fucosidosis | 3 |
| Mucopolysaccharidosis II | 3 |
| Mucopolysaccharidosis VII | 3 |
| Peroxisomal Disorders | 3 |
Trials
Showing 51 to 8 of 8. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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