Clinical trials
Phase 3 Mucopolysaccharidosis I trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
6 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 1 |
| 2001 | 1 |
| 2005 | 1 |
| 2008 | 1 |
| 2022 | 1 |
| 2023 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 4 |
| Active, not recruiting | 1 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Genzyme, a Sanofi Company | 3 |
| Aldagen | 1 |
| Cinnagen | 1 |
| Orchard Therapeutics | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis I | 6 |
| Mucopolysaccharidoses | 2 |
| Adrenoleukodystrophy | 1 |
| Canavan Disease | 1 |
| Fucosidosis | 1 |
| Gangliosidosis, GM1 | 1 |
| Leukodystrophy, Globoid Cell | 1 |
| Leukodystrophy, Metachromatic | 1 |
| Lysosomal Storage Diseases | 1 |
| Metabolism, Inborn Errors | 1 |
Trials
Showing 51 to 6 of 6. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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