Clinical trials
Terminated Mucopolysaccharidosis I trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
14 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2005 | 1 |
| 2008 | 4 |
| 2010 | 1 |
| 2011 | 2 |
| 2012 | 1 |
| 2014 | 2 |
| 2017 | 1 |
| 2019 | 1 |
| 2020 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Terminated | 14 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Masonic Cancer Center, University of Minnesota | 2 |
| Patricia I. Dickson, M.D. | 2 |
| Sangamo Therapeutics | 2 |
| Aldagen | 1 |
| Genzyme, a Sanofi Company | 1 |
| Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center | 1 |
| Magenta Therapeutics, Inc. | 1 |
| National MPS Society | 1 |
| Shire | 1 |
| Talaris Therapeutics Inc. | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis I | 14 |
| Mucopolysaccharidosis II | 6 |
| Mucopolysaccharidoses | 5 |
| Mucopolysaccharidosis VI | 5 |
| Leukodystrophy, Globoid Cell | 4 |
| Leukodystrophy, Metachromatic | 4 |
| Sudden Infant Death | 4 |
| Lysosomal Storage Diseases | 3 |
| alpha-Mannosidosis | 3 |
| Adrenoleukodystrophy | 2 |
Trials
Showing 51 to 14 of 14. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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