Clinical trials
Phase 1/2 Metabolic Diseases trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
29 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 1 |
| 2002 | 1 |
| 2007 | 1 |
| 2009 | 1 |
| 2011 | 1 |
| 2012 | 1 |
| 2013 | 4 |
| 2014 | 2 |
| 2015 | 1 |
| 2016 | 2 |
| 2017 | 1 |
| 2019 | 1 |
| 2020 | 1 |
| 2021 | 2 |
| 2022 | 4 |
| 2023 | 1 |
| 2024 | 2 |
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 11 |
| Recruiting | 7 |
| Terminated | 5 |
| Active, not recruiting | 2 |
| Withdrawn | 2 |
| Not yet recruiting | 1 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| ModernaTX, Inc. | 3 |
| 4D Molecular Therapeutics | 2 |
| LYSOGENE | 2 |
| Washington University School of Medicine | 2 |
| 89bio, Inc. | 1 |
| Alexion Pharmaceuticals, Inc. | 1 |
| Baylor College of Medicine | 1 |
| Diva De Leon | 1 |
| Eledon Pharmaceuticals | 1 |
| Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Metabolic Diseases | 29 |
| Genetic Diseases, Inborn | 10 |
| Lysosomal Storage Diseases | 6 |
| Metabolism, Inborn Errors | 6 |
| Nervous System Diseases | 5 |
| Central Nervous System Diseases | 4 |
| Diabetes Mellitus | 4 |
| Immune System Diseases | 4 |
| Mucopolysaccharidosis III | 4 |
| Autoimmune Diseases | 3 |
Trials
Showing 76 to 29 of 29. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
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