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Clinical trials

Metabolism, Inborn Errors trials in Brazil

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Metabolism, Inborn Errors Country / region: Brazil Clear all

6 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20071
20081
20141
20151
20211
20241

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed3
Recruiting1
Terminated1
Unknown status1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Kastle Therapeutics, LLC2
Alexion Pharmaceuticals, Inc.1
Intellia Therapeutics1
Protecting Brains Saving Futures1
Shire1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Metabolism, Inborn Errors6
Genetic Diseases, Inborn5
Metabolic Diseases5
Lipid Metabolism Disorders4
Infant, Newborn, Diseases3
Lipid Metabolism, Inborn Errors3
Congenital Abnormalities2
Dyslipidemias2
Homozygous Familial Hypercholesterolemia2
Hypercholesterolemia2

Trials

Showing 76 to 6 of 6. Each trial links to its page on Pharma Observatory.

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