Clinical trials
Metabolism, Inborn Errors trials with no applicable phase
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
29 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 2 |
| 2006 | 1 |
| 2011 | 1 |
| 2013 | 1 |
| 2014 | 1 |
| 2016 | 2 |
| 2017 | 2 |
| 2018 | 3 |
| 2019 | 2 |
| 2023 | 1 |
| 2024 | 3 |
| 2026 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 22 |
| Recruiting | 3 |
| Active, not recruiting | 1 |
| Not yet recruiting | 1 |
| Terminated | 1 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| National Center for Research Resources (NCRR) | 5 |
| Dr. Schär AG / SPA | 2 |
| FDA Office of Orphan Products Development | 2 |
| Rigshospitalet, Denmark | 2 |
| University of North Carolina, Chapel Hill | 2 |
| Vitaflo International, Ltd | 2 |
| Assistance Publique - Hôpitaux de Paris | 1 |
| Cliniques universitaires Saint-Luc- Université Catholique de Louvain | 1 |
| Fred Hutchinson Cancer Center | 1 |
| Manchester University NHS Foundation Trust | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Metabolism, Inborn Errors | 29 |
| Rare Diseases | 10 |
| Phenylketonurias | 7 |
| Genetic Diseases, Inborn | 6 |
| Metabolic Diseases | 5 |
| Sphingolipidoses | 3 |
| Adrenoleukodystrophy | 2 |
| Amino Acid Metabolism, Inborn Errors | 2 |
| Brain Diseases | 2 |
| Brain Diseases, Metabolic | 2 |
Trials
Showing 26 to 29 of 29. Each trial links to its page on Pharma Observatory.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
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