Clinical trials
Metabolism, Inborn Errors trials with unknown status
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
12 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2007 | 1 |
| 2008 | 1 |
| 2016 | 1 |
| 2017 | 1 |
| 2019 | 1 |
| 2021 | 1 |
| 2022 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Unknown status | 12 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| National Center for Research Resources (NCRR) | 4 |
| CENTOGENE GmbH Rostock | 1 |
| Celgene Corporation | 1 |
| Fairview University Medical Center | 1 |
| Mendel Tuchman | 1 |
| National Taiwan University Hospital | 1 |
| Protecting Brains Saving Futures | 1 |
| Rigshospitalet, Denmark | 1 |
| West Kazakhstan Medical University | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Metabolism, Inborn Errors | 12 |
| Rare Diseases | 5 |
| Gaucher Disease | 2 |
| Multiple Acyl Coenzyme A Dehydrogenase Deficiency | 2 |
| Sphingolipidoses | 2 |
| Acute Disease | 1 |
| Adrenoleukodystrophy | 1 |
| Amino Acid Metabolism, Inborn Errors | 1 |
| Anemia, Sickle Cell | 1 |
| Argininosuccinic Aciduria | 1 |
Trials
Showing 26 to 12 of 12. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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