Skip to content

Clinical trials

Mucopolysaccharidosis III trials in Germany

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Mucopolysaccharidosis III Country / region: Germany Clear all

14 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20121
20141
20152
20161
20173
20183
20201
20221
20231

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed6
Terminated3
Unknown status3
Active, not recruiting1
Enrolling by invitation1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Allievex Corporation5
Shire3
Abeona Therapeutics, Inc2
JCR Pharmaceuticals Co., Ltd.1
LYSOGENE1
Swedish Orphan Biovitrum1
University Hospital Heidelberg1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Mucopolysaccharidosis III14
Lysosomal Storage Diseases2
Mucopolysaccharidosis II2
Mental Disorders1
Mucopolysaccharidoses1
Mucopolysaccharidosis I1

Trials

Showing 26 to 14 of 14. Each trial links to its page on Pharma Observatory.

No trials match these filters.

Try a different keyword, or clear a filter.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.