Clinical trials
Active, not recruiting Mucopolysaccharidosis III trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
6 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2018 | 1 |
| 2020 | 1 |
| 2023 | 2 |
| 2024 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Active, not recruiting | 6 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| JCR Pharmaceuticals Co., Ltd. | 2 |
| Denali Therapeutics Inc. | 1 |
| GC Biopharma Corp | 1 |
| RTI International | 1 |
| University of Manchester | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis III | 6 |
| Anemia, Sickle Cell | 1 |
| Angelman Syndrome | 1 |
| Aortic Stenosis, Supravalvular | 1 |
| Argininosuccinic Aciduria | 1 |
| Barth Syndrome | 1 |
| Biotinidase Deficiency | 1 |
| Canavan Disease | 1 |
| Carbamoyl-Phosphate Synthase I Deficiency Disease | 1 |
| Citrullinemia | 1 |
Trials
Showing 26 to 6 of 6. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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