Clinical trials
Recruiting Mucopolysaccharidosis III trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
6 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2012 | 1 |
| 2016 | 1 |
| 2017 | 1 |
| 2024 | 2 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Recruiting | 6 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Institut National de la Santé Et de la Recherche Médicale, France | 1 |
| Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center | 1 |
| Ozlem Goker-Alpan | 1 |
| Phoenix Nest | 1 |
| Ultragenyx Pharmaceutical Inc | 1 |
| University of Pittsburgh | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis III | 6 |
| Mucopolysaccharidosis IV | 2 |
| Multiple Sulfatase Deficiency Disease | 2 |
| Gaucher Disease | 1 |
| Leukodystrophy, Globoid Cell | 1 |
| Leukoencephalopathies | 1 |
| Lysosomal Storage Diseases | 1 |
| Mucopolysaccharidosis I | 1 |
| Mucopolysaccharidosis II | 1 |
| Mucopolysaccharidosis VI | 1 |
Trials
Showing 51 to 6 of 6. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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