Clinical trials
Mucopolysaccharidosis IV trials in Canada
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
21 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2008 | 1 |
| 2009 | 1 |
| 2010 | 1 |
| 2011 | 2 |
| 2012 | 1 |
| 2013 | 2 |
| 2014 | 1 |
| 2016 | 1 |
| 2019 | 3 |
| 2020 | 2 |
| 2021 | 1 |
| 2023 | 1 |
| 2024 | 1 |
| 2025 | 2 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 13 |
| Enrolling by invitation | 3 |
| Recruiting | 2 |
| Terminated | 2 |
| Unknown status | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| QED Therapeutics, a BridgeBio company | 8 |
| BioMarin Pharmaceutical | 5 |
| The Canadian College of Naturopathic Medicine | 2 |
| BIO-CAT Microbials, LLC | 1 |
| Children's Hospital of Eastern Ontario | 1 |
| Ciusss de L'Est de l'Île de Montréal | 1 |
| MSP Starch Products Inc. | 1 |
| University of British Columbia | 1 |
| University of Minnesota | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis IV | 21 |
| Bone Diseases | 8 |
| Musculoskeletal Diseases | 8 |
| Osteochondrodysplasias | 8 |
| Dwarfism | 7 |
| Genetic Diseases, Inborn | 7 |
| Achondroplasia | 5 |
| Lysosomal Storage Diseases | 4 |
| Constipation | 3 |
| Diarrhea | 3 |
Trials
Showing 51 to 21 of 21. Each trial links to its page on Pharma Observatory.
No trials match these filters.
Try a different keyword, or clear a filter.
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
No changes to these trials in the last 7 days.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.