Clinical trials
Mucopolysaccharidosis IV trials in France
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
19 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2006 | 1 |
| 2008 | 1 |
| 2011 | 2 |
| 2014 | 1 |
| 2016 | 1 |
| 2017 | 1 |
| 2018 | 1 |
| 2019 | 1 |
| 2020 | 2 |
| 2021 | 1 |
| 2022 | 1 |
| 2023 | 1 |
| 2024 | 1 |
| 2025 | 2 |
| 2026 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 10 |
| Recruiting | 5 |
| Enrolling by invitation | 3 |
| Terminated | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| QED Therapeutics, a BridgeBio company | 7 |
| BioMarin Pharmaceutical | 4 |
| GOIZET | 1 |
| Innoskel | 1 |
| Institut National de la Santé Et de la Recherche Médicale, France | 1 |
| Lille Catholic University | 1 |
| Merck KGaA, Darmstadt, Germany | 1 |
| NTC srl | 1 |
| University Hospital, Angers | 1 |
| University Hospital, Montpellier | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis IV | 19 |
| Bone Diseases | 8 |
| Dwarfism | 7 |
| Genetic Diseases, Inborn | 7 |
| Musculoskeletal Diseases | 7 |
| Osteochondrodysplasias | 7 |
| Achondroplasia | 4 |
| Lysosomal Storage Diseases | 3 |
| Blind Loop Syndrome | 1 |
| Bone Diseases, Developmental | 1 |
Trials
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