Clinical trials
Mucopolysaccharidosis IV trials in Germany
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
9 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2008 | 1 |
| 2011 | 2 |
| 2012 | 2 |
| 2018 | 1 |
| 2019 | 1 |
| 2020 | 2 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 4 |
| Terminated | 3 |
| Unknown status | 1 |
| Withdrawn | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| BioMarin Pharmaceutical | 5 |
| CENTOGENE GmbH Rostock | 1 |
| NTC srl | 1 |
| QED Therapeutics, a BridgeBio company | 1 |
| SphinCS Lyso Gemeinnutzige UG (Haftungsbeschrankt) | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis IV | 9 |
| Lysosomal Storage Diseases | 5 |
| Achondroplasia | 1 |
| Bone Diseases | 1 |
| Dwarfism | 1 |
| Gangliosidoses | 1 |
| Gangliosidoses, GM2 | 1 |
| Gangliosidosis, GM1 | 1 |
| Genetic Diseases, Inborn | 1 |
| Mucolipidoses | 1 |
Trials
Showing 26 to 9 of 9. Each trial links to its page on Pharma Observatory.
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