Clinical trials
Mucopolysaccharidosis IV trials in Italy
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
12 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2008 | 1 |
| 2011 | 3 |
| 2014 | 1 |
| 2019 | 1 |
| 2020 | 3 |
| 2021 | 2 |
| 2023 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 7 |
| Terminated | 3 |
| Enrolling by invitation | 1 |
| Recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| BioMarin Pharmaceutical | 5 |
| QED Therapeutics, a BridgeBio company | 3 |
| Pfizer | 2 |
| Luca Sangiorgi | 1 |
| NTC srl | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Mucopolysaccharidosis IV | 12 |
| Achondroplasia | 5 |
| Bone Diseases | 4 |
| Genetic Diseases, Inborn | 4 |
| Lysosomal Storage Diseases | 4 |
| Musculoskeletal Diseases | 4 |
| Osteochondrodysplasias | 4 |
| Dwarfism | 3 |
Trials
Showing 76 to 12 of 12. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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