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Clinical trials

Terminated Mucopolysaccharidosis IV trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Mucopolysaccharidosis IV Status: Terminated Clear all

10 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20061
20081
20101
20111
20123
20151
20201
20211

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Terminated10

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
BioMarin Pharmaceutical4
Pfizer2
Clínica de Hidroterapia e Recuperacao Funcional1
Emory University1
National MPS Society1
Weill Medical College of Cornell University1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Mucopolysaccharidosis IV10
Lysosomal Storage Diseases4
Achondroplasia2
Bone Diseases1
Dwarfism1
Genetic Diseases, Inborn1
Mucopolysaccharidoses1
Mucopolysaccharidosis I1
Mucopolysaccharidosis II1
Mucopolysaccharidosis VI1

Trials

Showing 26 to 10 of 10. Each trial links to its page on Pharma Observatory.

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Recently changed trials

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