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Clinical trials

Muscular Diseases trials in Australia

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Diseases Country / region: Australia Clear all

18 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20091
20131
20141
20151
20172
20212
20223
20233
20241
20251
20262

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed8
Active, not recruiting4
Recruiting3
Terminated2
Enrolling by invitation1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Novartis Pharmaceuticals3
PTC Therapeutics3
Calcilytix Therapeutics, Inc., a BridgeBio company2
Vertex Pharmaceuticals Incorporated2
Abcuro, Inc.1
Avidity Biosciences, Inc.1
Endo USA Inc., a Keenova Therapeutics Company1
Kyntra Bio1
Pharming Technologies B.V.1
Stealth BioTherapeutics Inc.1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Diseases18
Musculoskeletal Diseases10
Nervous System Diseases8
Neuromuscular Diseases8
Genetic Diseases, Inborn7
Muscular Disorders, Atrophic7
Muscular Dystrophies7
Muscular Dystrophy, Duchenne5
Genetic Diseases, X-Linked4
Bulbo-Spinal Atrophy, X-Linked3

Trials

Showing 51 to 18 of 18. Each trial links to its page on Pharma Observatory.

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Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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