Skip to content

Clinical trials

Phase 1/2 Muscular Diseases trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Diseases Phase: Phase 1/2 Clear all

10 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20122
20142
20151
20161
20221
20242

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed4
Withdrawn2
Active, not recruiting1
Not yet recruiting1
Recruiting1
Unknown status1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
National Human Genome Research Institute (NHGRI)2
Chaitanya Hospital, Pune1
Craig McDonald, MD1
Dynacure1
George Washington University1
National Institute of Nursing Research (NINR)1
Texas Tech University Health Sciences Center1
University Health Network, Toronto1
Vertex Pharmaceuticals Incorporated1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Diseases10
Neuromuscular Diseases3
Mitochondrial Diseases2
Muscular Dystrophies2
Muscular Dystrophy, Duchenne2
Musculoskeletal Diseases2
Nervous System Diseases2
Acidosis, Lactic1
Anxiety Disorders1
Cardiomyopathies1

Trials

Showing 26 to 10 of 10. Each trial links to its page on Pharma Observatory.

No trials match these filters.

Try a different keyword, or clear a filter.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.