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Clinical trials

Muscular Dystrophies trials in the United States

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophies Country / region: United States Clear all

126 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20002
20011
20041
20052
20062
20073
20082
20094
20106
20116
20126
20137
20144
20157
20163
20173
20186
20196
20204
20214
202213
202310
20245
20256
20267

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed60
Recruiting27
Terminated15
Active, not recruiting12
Unknown status5
Enrolling by invitation3
Withdrawn1
Available1
Not yet recruiting1
No longer available1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Cooperative International Neuromuscular Research Group8
National Institute of Neurological Disorders and Stroke (NINDS)5
Avidity Biosciences, Inc.4
Virginia Commonwealth University4
Wake Forest University Health Sciences4
Capricor Inc.3
Catabasis Pharmaceuticals3
Cedars-Sinai Medical Center3
Fulcrum Therapeutics3
GlaxoSmithKline3

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophies126
Muscular Dystrophy, Duchenne56
Neuromuscular Diseases26
Muscular Diseases18
Musculoskeletal Diseases18
Spinal Cord Injuries17
Nervous System Diseases15
Amyotrophic Lateral Sclerosis14
Genetic Diseases, Inborn14
Muscular Disorders, Atrophic13

Trials

Showing 26 to 50 of 126. Each trial links to its page on Pharma Observatory.

26 more trials match. See them on Pharma Observatory

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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