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Clinical trials

Muscular Dystrophies trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophies Clear all

222 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20002
20012
20031
20041
20052
20063
20073
20084
20096
20109
201110
20128
201310
201413
201512
20168
20179
201813
201913
202010
20219
202221
202314
20248
20258
202614

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed107
Recruiting37
Unknown status26
Terminated20
Active, not recruiting16
Withdrawn6
Enrolling by invitation5
Not yet recruiting2
No longer available1
Available1
Approved for marketing1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Cooperative International Neuromuscular Research Group8
GlaxoSmithKline7
Avidity Biosciences, Inc.5
National Institute of Neurological Disorders and Stroke (NINDS)5
Rigshospitalet, Denmark5
Fulcrum Therapeutics4
IRCCS Eugenio Medea4
Virginia Commonwealth University4
Wake Forest University Health Sciences4
BioMarin Pharmaceutical3

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophies222
Muscular Dystrophy, Duchenne89
Neuromuscular Diseases41
Muscular Diseases29
Musculoskeletal Diseases23
Spinal Cord Injuries23
Amyotrophic Lateral Sclerosis19
Nervous System Diseases19
Genetic Diseases, Inborn18
Myotonic Dystrophy18

Trials

Showing 26 to 50 of 222. Each trial links to its page on Pharma Observatory.

122 more trials match. See them on Pharma Observatory

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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