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Clinical trials

Phase 3 Muscular Dystrophies trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophies Phase: Phase 3 Clear all

21 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20041
20071
20091
20101
20111
20133
20142
20151
20171
20181
20191
20212
20222
20262

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed10
Terminated7
Recruiting2
Active, not recruiting1
Withdrawn1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
GlaxoSmithKline3
PTC Therapeutics3
Catabasis Pharmaceuticals2
Cooperative International Neuromuscular Research Group2
Avidity Biosciences, Inc.1
BioMarin Pharmaceutical1
Bioblast Pharma Ltd.1
Capricor Inc.1
Dyne Therapeutics1
Fulcrum Therapeutics1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophies21
Muscular Dystrophy, Duchenne18
Neuromuscular Diseases11
Genetic Diseases, Inborn8
Musculoskeletal Diseases8
Genetic Diseases, X-Linked6
Muscular Diseases6
Muscular Disorders, Atrophic6
Nervous System Diseases6
Myotonic Dystrophy2

Trials

Showing 26 to 21 of 21. Each trial links to its page on Pharma Observatory.

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Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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