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Clinical trials

Phase 1/2 Muscular Dystrophies trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Muscular Dystrophies Phase: Phase 1/2 Clear all

11 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20051
20142
20152
20161
20232
20241
20251
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed4
Active, not recruiting3
Unknown status2
Recruiting1
Terminated1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Chaitanya Hospital, Pune2
AskBio Inc1
Avidity Biosciences, Inc.1
Catabasis Pharmaceuticals1
Cooperative International Neuromuscular Research Group1
Epicrispr Biotechnologies, Inc.1
Hoffmann-La Roche1
Jerry R. Mendell1
Precision BioSciences, Inc.1
Vertex Pharmaceuticals Incorporated1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Muscular Dystrophies11
Muscular Dystrophy, Duchenne6
Muscular Diseases2
Muscular Dystrophy, Facioscapulohumeral2
Musculoskeletal Diseases2
Nervous System Diseases2
Neuromuscular Diseases2
Genetic Diseases, Inborn1
Heredodegenerative Disorders, Nervous System1
Muscular Disorders, Atrophic1

Trials

Showing 76 to 11 of 11. Each trial links to its page on Pharma Observatory.

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Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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