Clinical trials
Phase 1/2 Myotonic Dystrophy trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
8 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2005 | 1 |
| 2014 | 1 |
| 2021 | 1 |
| 2022 | 1 |
| 2024 | 3 |
| 2025 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 3 |
| Active, not recruiting | 2 |
| Recruiting | 2 |
| Enrolling by invitation | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| ARTHEx Biotech S.L. | 1 |
| Avidity Biosciences, Inc. | 1 |
| Dyne Therapeutics | 1 |
| Ionis Pharmaceuticals, Inc. | 1 |
| Sanofi | 1 |
| Sarepta Therapeutics, Inc. | 1 |
| University of Rochester | 1 |
| Vertex Pharmaceuticals Incorporated | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Myotonic Dystrophy | 8 |
| Myotonic Disorders | 2 |
| Neuromuscular Diseases | 2 |
| Genetic Diseases, Inborn | 1 |
| Heredodegenerative Disorders, Nervous System | 1 |
| Muscular Diseases | 1 |
| Muscular Disorders, Atrophic | 1 |
| Muscular Dystrophies | 1 |
| Musculoskeletal Diseases | 1 |
| Myotonia | 1 |
Trials
Showing 76 to 8 of 8. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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