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Clinical trials

Observational Congenital, Hereditary, and Neonatal Diseases and Abnormalities trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Congenital, Hereditary, and Neonatal Diseases and Abnormalities Phase: Observational Clear all

79 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20002
20015
20028
20031
20046
20057
20065
20073
20082
20101
20121
20161
20172
20181
20191
20202
20211
20223
20232
20241
20252
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Terminated38
Completed29
Recruiting7
Unknown status2
Withdrawn2
Active, not recruiting1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Children's Healthcare of Atlanta49
Emory University10
G. d'Annunzio University2
Bispebjerg Hospital1
Children's Hospital of Philadelphia1
Erasmus Medical Center1
George Washington University1
Hacettepe University1
Hadassah Medical Organization1
Hong Kong Children's Hospital1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Congenital, Hereditary, and Neonatal Diseases and Abnormalities79
Heart Defects, Congenital8
Genetic Diseases, Inborn4
Congenital Abnormalities2
Cyanosis2
Down Syndrome2
Heart Failure2
Intellectual Disability2
Metabolic Diseases2
Metabolism, Inborn Errors2

Trials

Showing 26 to 50 of 79. Each trial links to its page on Pharma Observatory.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

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