Clinical trials
Neuromuscular Diseases trials in the United States
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
118 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2000 | 1 |
| 2001 | 3 |
| 2002 | 1 |
| 2003 | 1 |
| 2005 | 1 |
| 2006 | 1 |
| 2008 | 2 |
| 2009 | 4 |
| 2010 | 3 |
| 2011 | 4 |
| 2012 | 1 |
| 2013 | 6 |
| 2014 | 5 |
| 2015 | 6 |
| 2016 | 5 |
| 2017 | 6 |
| 2018 | 5 |
| 2019 | 7 |
| 2020 | 5 |
| 2021 | 9 |
| 2022 | 7 |
| 2023 | 4 |
| 2024 | 9 |
| 2025 | 10 |
| 2026 | 9 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 61 |
| Recruiting | 25 |
| Terminated | 15 |
| Active, not recruiting | 8 |
| Not yet recruiting | 3 |
| Unknown status | 3 |
| Available | 1 |
| Withdrawn | 1 |
| Enrolling by invitation | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| National Institute of Neurological Disorders and Stroke (NINDS) | 10 |
| Columbia University | 9 |
| Catabasis Pharmaceuticals | 3 |
| Fulcrum Therapeutics | 3 |
| National Institute of Nursing Research (NINR) | 3 |
| PTC Therapeutics | 3 |
| Scholar Rock, Inc. | 3 |
| University of Pennsylvania | 3 |
| Amylyx Pharmaceuticals Inc. | 2 |
| Avidity Biosciences, Inc. | 2 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Neuromuscular Diseases | 118 |
| Nervous System Diseases | 30 |
| Muscular Dystrophies | 26 |
| Musculoskeletal Diseases | 25 |
| Muscular Diseases | 24 |
| Muscular Dystrophy, Duchenne | 20 |
| Amyotrophic Lateral Sclerosis | 18 |
| Genetic Diseases, Inborn | 16 |
| Muscular Atrophy, Spinal | 16 |
| Neurodegenerative Diseases | 14 |
Trials
Showing 26 to 50 of 118. Each trial links to its page on Pharma Observatory.
18 more trials match. See them on Pharma Observatory
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
Go deeper on Pharma Observatory
Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.