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Clinical trials

Phase 2 Neuromuscular Diseases trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Neuromuscular Diseases Phase: Phase 2 Clear all

23 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20101
20111
20132
20162
20173
20181
20193
20201
20221
20243
20253
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed9
Terminated7
Recruiting3
Withdrawn1
Not yet recruiting1
Enrolling by invitation1
Active, not recruiting1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Fulcrum Therapeutics3
PepGen Inc3
Flex Pharma, Inc.2
Afasci Inc1
Amylyx Pharmaceuticals Inc.1
Avidity Biosciences, Inc.1
Capricor Inc.1
Centre d'Investigation Clinique et Technologique 8051
Craig McDonald, MD1
Emory University1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Neuromuscular Diseases23
Muscular Dystrophies9
Nervous System Diseases9
Musculoskeletal Diseases6
Neurodegenerative Diseases6
Amyotrophic Lateral Sclerosis5
Muscular Dystrophy, Duchenne5
Genetic Diseases, Inborn4
Muscular Diseases4
Muscular Disorders, Atrophic4

Trials

Showing 51 to 23 of 23. Each trial links to its page on Pharma Observatory.

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Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

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