Clinical trials
Observational Neuromuscular Diseases trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
141 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2001 | 3 |
| 2002 | 1 |
| 2003 | 1 |
| 2004 | 1 |
| 2005 | 1 |
| 2006 | 1 |
| 2007 | 1 |
| 2008 | 2 |
| 2009 | 4 |
| 2010 | 1 |
| 2011 | 4 |
| 2012 | 1 |
| 2013 | 2 |
| 2014 | 11 |
| 2015 | 9 |
| 2016 | 5 |
| 2017 | 2 |
| 2018 | 6 |
| 2019 | 12 |
| 2020 | 10 |
| 2021 | 11 |
| 2022 | 9 |
| 2023 | 9 |
| 2024 | 12 |
| 2025 | 11 |
| 2026 | 10 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 73 |
| Recruiting | 32 |
| Unknown status | 15 |
| Not yet recruiting | 7 |
| Active, not recruiting | 4 |
| Enrolling by invitation | 4 |
| Terminated | 4 |
| Withdrawn | 2 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Centre d'Investigation Clinique et Technologique 805 | 10 |
| Columbia University | 8 |
| National Institute of Neurological Disorders and Stroke (NINDS) | 8 |
| Assistance Publique - Hôpitaux de Paris | 5 |
| Hospices Civils de Lyon | 5 |
| University Hospital, Bordeaux | 4 |
| Boston Children's Hospital | 2 |
| Corporacion Parc Tauli | 2 |
| Guy's and St Thomas' NHS Foundation Trust | 2 |
| Istanbul University - Cerrahpasa | 2 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Neuromuscular Diseases | 141 |
| Muscular Atrophy, Spinal | 16 |
| Amyotrophic Lateral Sclerosis | 12 |
| Muscular Dystrophies | 11 |
| Muscular Dystrophy, Duchenne | 10 |
| Motor Neuron Disease | 8 |
| Nervous System Diseases | 8 |
| Muscular Diseases | 6 |
| Myasthenia Gravis | 6 |
| Peripheral Nervous System Diseases | 6 |
Trials
Showing 76 to 100 of 141. Each trial links to its page on Pharma Observatory.
41 more trials match. See them on Pharma Observatory
Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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