Skip to content

Clinical trials

Phase 1 Neuromuscular Diseases trials

Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.

Filters: Condition: Neuromuscular Diseases Phase: Phase 1 Clear all

15 trials match Source: ClinicalTrials.gov registrations

Trials started per year

By phase, 2000 to 2026.

Trials started per year
CategoryTrials
20051
20061
20123
20151
20171
20181
20221
20232
20241
20252
20261

Status

Trials by registry status. Select a bar to filter.

Trials by status
CategoryTrials
Completed8
Not yet recruiting3
Unknown status3
Recruiting1

Top lead sponsors

A sponsor with a page on Pharma Observatory links to it.

Top lead sponsors
CategoryTrials
Hanyang University Seoul Hospital2
Adjuvia Therapeutics, Inc.1
AstraZeneca1
Brain Trust Bio1
Cabaletta Bio1
Edgewise Therapeutics, Inc.1
Genethon1
Hospital Sao Joao1
Johns Hopkins University1
Peking University Third Hospital1

Top conditions

MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.

Top conditions
CategoryTrials
Neuromuscular Diseases15
Nervous System Diseases7
Musculoskeletal Diseases6
Muscular Diseases5
Amyotrophic Lateral Sclerosis4
Motor Neuron Disease4
Neurodegenerative Diseases4
Central Nervous System Diseases3
Genetic Diseases, Inborn3
Muscular Dystrophies3

Trials

Showing 76 to 15 of 15. Each trial links to its page on Pharma Observatory.

No trials match these filters.

Try a different keyword, or clear a filter.

Recently changed trials

Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.

No changes to these trials in the last 7 days.

Go deeper on Pharma Observatory

Pharma Observatory connects clinical trials, sponsors, sites and investigators in one searchable platform.