Clinical trials
Phase 2 Neuromuscular Diseases trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
23 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2010 | 1 |
| 2011 | 1 |
| 2013 | 2 |
| 2016 | 2 |
| 2017 | 3 |
| 2018 | 1 |
| 2019 | 3 |
| 2020 | 1 |
| 2022 | 1 |
| 2024 | 3 |
| 2025 | 3 |
| 2026 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Completed | 9 |
| Terminated | 7 |
| Recruiting | 3 |
| Withdrawn | 1 |
| Not yet recruiting | 1 |
| Enrolling by invitation | 1 |
| Active, not recruiting | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Fulcrum Therapeutics | 3 |
| PepGen Inc | 3 |
| Flex Pharma, Inc. | 2 |
| Afasci Inc | 1 |
| Amylyx Pharmaceuticals Inc. | 1 |
| Avidity Biosciences, Inc. | 1 |
| Capricor Inc. | 1 |
| Centre d'Investigation Clinique et Technologique 805 | 1 |
| Craig McDonald, MD | 1 |
| Emory University | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Neuromuscular Diseases | 23 |
| Muscular Dystrophies | 9 |
| Nervous System Diseases | 9 |
| Musculoskeletal Diseases | 6 |
| Neurodegenerative Diseases | 6 |
| Amyotrophic Lateral Sclerosis | 5 |
| Muscular Dystrophy, Duchenne | 5 |
| Genetic Diseases, Inborn | 4 |
| Muscular Diseases | 4 |
| Muscular Disorders, Atrophic | 4 |
Trials
Showing 76 to 23 of 23. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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