Clinical trials
Expanded access Thalassemia trials
Search ClinicalTrials.gov registrations by keyword, then narrow by condition, phase, status, country and start year.
2 trials match Source: ClinicalTrials.gov registrations
Trials started per year
By phase, 2000 to 2026.
| Category | Trials |
|---|---|
| 2006 | 1 |
Status
Trials by registry status. Select a bar to filter.
| Category | Trials |
|---|---|
| Approved for marketing | 1 |
| Available | 1 |
Top lead sponsors
A sponsor with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Children's Hospital of Philadelphia | 1 |
| Joanne Kurtzberg, MD | 1 |
Top conditions
MeSH conditions the trials were registered with, not their broader categories. A condition with a page on Pharma Observatory links to it.
| Category | Trials |
|---|---|
| Thalassemia | 2 |
| Adrenoleukodystrophy | 1 |
| Anemia, Aplastic | 1 |
| Anemia, Sickle Cell | 1 |
| Hematologic Neoplasms | 1 |
| Immunologic Deficiency Syndromes | 1 |
| Iron Overload | 1 |
| Leukemia, Myeloid, Acute | 1 |
| Lymphoma | 1 |
| Metabolic Diseases | 1 |
Trials
Showing 26 to 2 of 2. Each trial links to its page on Pharma Observatory.
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Recently changed trials
Changes observed in the last 7 days, newest first, site-count changes left out. Source: ClinicalTrials.gov.
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